Genome Medicine


Musings

Musings on genome medicine: gene therapy

David G Nathan* and Stuart H Orkin

Author Affiliations

Dana-Farber Cancer Institute, Binney Street, Boston, MA 02115, USA.

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Genome Med 2009, 1:38 doi:10.1186/gm38

Published: 3 April 2009

Abstract

Though the field has moved with glacial speed, gene therapies have been carried out successfully in patients with bone marrow disorders including immune deficiencies. The field may be poised to move forward more rapidly, but many barriers have yet to be surmounted.